For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...

Dr. Matthew Matasar discusses why stem cell transplant is still a standard, life-saving option in blood cancers and how CAR-T ...

Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...

The Schafluetzel family says they’re grateful for the community’s support, as Ella will be heading to Duke this Sunday to ...

Kids with a rare bone cancer called Ewing sarcoma might live longer if prescribed pazopanib, a drug that blocks blood supply ...

A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...

Judge says state can't call attempted arrest of Melissa Perez 'unlawful' Trump instructs Pentagon to ensure troops are paid ...

New research found that gene therapy for children with "bubble boy disease," or SCID, was successful in 95% of trial ...

Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...

Maulana Siddiq Patel appears in the video launched by charity One voice Blackburn and the Anthony Nolan trust.