Comedian Gilbert Gottfried, shown in a 2016 photo, died on Tuesday, April 12, from recurrent ventricular tachycardia due to myotonic dystrophy type II. Scott Roth Scott Roth/Invision/AP Comedian ...

Myotonic dystrophy type 1 incurs high healthcare costs, driven by age and comorbidities like cardiac and respiratory issues. Early detection and integrated management of multisystemic complications ...

- Patient-reported outcomes support clinical meaningfulness of improvements in function and strength - - Meaningful improvements in overall disease burden reported by both patients and physicians - ...

AOC 1001 continues to be generally well tolerated; Avidity provides more information on the rare serious adverse event in a single participant that led to the partial clinical hold AOC 1001 top-line ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Back to Healio A Southern California biopharmaceutical ...

Please provide your email address to receive an email when new articles are posted on . You've successfully added to your alerts. You will receive an email when new content is published. Click Here to ...

The FDA has cleared Avidity Biosciences (NASDAQ:RNA) to proceed with the Phase 1/2 MARINA clinical trial of AOC 1001 in adults with myotonic dystrophy type 1 (DM1). The Phase 1/2 clinical trial ...

Dyne Therapeutics announces FDA Fast Track designation for DYNE-101, targeting myotonic dystrophy type 1 with potential accelerated approval in 2026. Dyne Therapeutics has announced that its ...

Comedian Gilbert Gottfried died on Tuesday after a long illness, his family announced. His publicist revealed in a statement to multiple publications, including People, that Gottfried had “recurrent ...