A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...

Faulty versions of the LMNA gene can cause a wide range of health problems, including heart muscle disease (dilated ...

MIT scientists have found a way to make gene editing far safer and more accurate — a breakthrough that could reshape how we ...

Researchers have developed a DNA-based therapy that targets the PCSK9 gene to lower cholesterol naturally. Using polypurine ...

Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side effects. Early results show dramatic reductions in cholesterol levels, offering ...

Gene therapy for some diseases, including Duchenne muscular dystrophy (DMD), can be tricky because the needed gene is often too large to fit inside the viral vector used for delivery. Researchers at ...

Decades ago, researchers showed that Down syndrome (also known as trisomy 21), was caused when individuals carried an extra copy of chromosome 21. Down syndrome is also the most common genetic cause ...

For more than a decade, the strongest AIDS drugs could not fully control Matt Chappell's HIV infection. Now his body controls it by itself, and researchers are trying to perfect the gene editing that ...

A new DNA-based therapy could cut cholesterol nearly in half—without relying on statins or causing side effects.

Growing use of CAR-T therapy for large B-cell lymphoma, gene delivery innovations to solid lesions, and growing investor interest are driving the cancer gene therapy industry forwardAustin, Oct. 23, ...

A research team has developed a high-throughput multiplexed gene and cell doping analysis (HiMDA) based on gene scissors (CRISPR-Cas). The work is published in the journal Science Advances. Unethical ...